Cost-Effectiveness of Advanced Therapy Medicinal Products
Building tools to make important decisions.
Cost-Effectiveness of Advanced Therapy Medicinal Products
Building tools to make important decisions.
The overall aim of this project is to undertake theoretical work and empirical studies related to the economic evaluation of a novel class of health technologies known as Advanced Therapy Medicinal Products (ATMP). These include gene therapy, cell therapy and regenerative medicine. ATMP are used to treat rare diseases, sometimes offering a cure for patients who cannot be treated in any other way. However, many fail to break through into commercial success, representing a waste of research resources, and those that do often charge extremely high prices.
Establish working guidelines for investment decisions (go/no go) by private and public investors in these therapies at distinct points in the life cycle
Recommend clear, consensual and practical criteria that decision makers in the national health service can use for establishing the price of such therapies and whether they should be financed in the NHS
Consider the theoretical and practical merits of distinct options for how such therapies might be reimbursed, for example, through risk-sharing schemes
| Name | Info | |
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| Research group (N=7) | ||
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David M. Epstein | PhD. Professor at University of Granada. Tasks: Principal Investigator and coordinator of the work packages. Person-months in project: 7 |
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Jaime Espín Balbino | PhD. Professor, EASP. Specialist in pharmaceutical pricing and reimbursement policy. Task Leader: P&R (3.5 and 4.7). Person-months in project: 3 |
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Antonio Orly de Labry Lima | PhD. Qualified pharmacist and health sciences researcher, EASP. Leader for CEA, societal impact and SROI (WP 3 and 4). Person-months in project: 3 |
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Roke I. Oruezabal Guijarro | PhD. Masters. Head of Innovation & Development, And&tAT. Leader for consultation with experts (Task 1.2), stakeholder analysis (WP2), case studies (4.1 and 4.2), validation (WP5). Person-months in project: 3 |
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Juan C. Rejón Parrilla | Masters. Qualified pharmacist and Senior Economist, AETSA. Expert in health policy. Leader for innovation (3.3 & 4.5). Person-months in project:3 |
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Rosario Mata Alcazar-Caballero | Doctor in Medicine. Clinical scientist, And&tAT. Leader for stakeholder analysis (WP2), case studies (4.1) and ethics (6.2). Person-months in project: 3 |
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Juan Antonio Blasco | Doctor in Preventative Medicine & Public Health. Scientific coordinator, AETSA. Task leader: Literature review (1.1), and implementation (4.8). Person-months in project: 3 |
| Name | Info | |
|---|---|---|
| Work group (N=9) | ||
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Marta Trapero-Bertran | PhD. Professor of Economics at UIC, Barcelona. Expert in health economics and health policy. Task: Member of expert advisory group. Person-months in project: 0.5 |
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Richard Grieve | PhD. Professor of Health Economic Methodology, London School of Hygiene and Tropical Medicine. Task: Member of expert advisory group. Person-months in project: 0.5 |
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Marta Ortega-Ortega | PhD. Professor at Complutense University, Madrid. Expert on health economic costs and impact of diseases on productivity. Task: Support for impact of therapies on work productivity and social costs. Person-months in project: 1.5 |
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Leticia García-Monchón | PhD. Researcher, EASP. Expert on quantitative methods and decision modelling in health service research. Task: Support for SROI and CEA. Person-months in project: 3 |
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Blanca Quijano | Masters. Qualified pharmacist and Project manager And&tAT. Task: Support for case studies WP4. Person-months in project: 3 |
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Daniel Pérez Troncoso | Masters. Phd Student and investigator, UGR. Task: support for methodological development, evidence collection and modelling work and website design, management. Person-months in project: 6 |
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Modou Diop Wayal | Masters. Phd Student and investigator, UGR. Task: support for methodological development, evidence collection and modelling work. Person-months in project: 6 |
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Lorena Aguilera | Masters. Biotechnology scientist, AETSA. Task: Support for literature review. Person-months in project: 6 |
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Ángela Ponce | Masters. Technological Translation & Development Technician, And&tAT. Task: Support for social return on investment. Person-months in project: 6 |
This project has been funded by
